Leber's Congenital Amaurosis Archives - Board Certified Eye Doctors

Luxturna | First Gene Therapy Treats Blindness

By Gregory H. Scimeca, M.D. | May 14, 2018

Luxturna Gene Therapy Treats Blindness | Burlington County Eye Physicians

First patient to receive Luxturna was a 13 year old boy with Leber’s congenital amaurosis, a heritable form of blindness due to defective copies of RPE65 genes.